The identification of hematopoietic-specific regulatory elements for WASp gene expression

by Jun Zhan, Irudayam Maria Johnson, Matthew Wielgosz, Arthur W Nienhuis
Published 2016-01-01

Safe and Effective Gene Therapy for Murine Wiskott-Aldrich Syndrome Using an Insulated Lentiviral Vector

by Swati Singh, Iram Khan, Socheath Khim, Brenda Seymour, Karen Sommer, Matthew Wielgosz, Zachary Norgaard, Hans-Peter Kiem, Jennifer Adair, Denny Liggitt, Arthur Nienhuis, David J. Rawlings
Published 2017-03-01