Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction

by Sang-oh Han, Giuseppe Ronzitti, Benjamin Arnson, Christian Leborgne, Songtao Li, Federico Mingozzi, Dwight Koeberl
Published 2017-03-01

Polyubiquitin is required for growth, development and pathogenicity in the rice blast fungus Magnaporthe oryzae.

by Yeonyee Oh, William L Franck, Sang-Oh Han, Angela Shows, Emine Gokce, David C Muddiman, Ralph A Dean
Published 2012-01-01

Three-dimensional tissue-engineered human skeletal muscle model of Pompe disease

by Jason Wang, Chris J. Zhou, Alastair Khodabukus, Sabrina Tran, Sang-Oh Han, Aaron L. Carlson, Lauran Madden, Priya S. Kishnani, Dwight D. Koeberl, Nenad Bursac
Published 2021-05-01

Comparisons of Infant and Adult Mice Reveal Age Effects for Liver Depot Gene Therapy in Pompe Disease

by Sang-oh Han, Songtao Li, Angela McCall, Benjamin Arnson, Jeffrey I. Everitt, Haoyue Zhang, Sarah P. Young, Mai K. ElMallah, Dwight D. Koeberl
Published 2020-06-01