Essential list of medicinal products for rare diseases: recommendations from the IRDiRC Rare Disease Treatment Access Working Group

by William A. Gahl, Durhane Wong-Rieger, Virginie Hivert, Rachel Yang, Galliano Zanello, Stephen Groft
Published 2021-07-01

The use or generation of biomedical data and existing medicines to discover and establish new treatments for patients with rare diseases – recommendations of the IRDiRC Data Mining...

by Noel T Southall, Madhusudan Natarajan, Lilian Pek Lian Lau, Anneliene Hechtelt Jonker, Benoît Deprez, Tim Guilliams, Lawrence Hunter, Carin MA Rademaker, Virginie Hivert, Diego Ardigò, on behalf of the IRDiRC Data Mining and Repurposing Task Force
Published 2019-10-01

Barriers to the conduct of randomised clinical trials within all disease areas

by Snezana Djurisic, Ana Rath, Sabrina Gaber, Silvio Garattini, Vittorio Bertele, Sandra-Nadia Ngwabyt, Virginie Hivert, Edmund A. M. Neugebauer, Martine Laville, Michael Hiesmayr, Jacques Demotes-Mainard, Christine Kubiak, Janus C. Jakobsen, Christian Gluud
Published 2017-08-01

Evaluating the “return on patient engagement initiatives” in medicines research and development: A literature review

by Lidewij Eva Vat, Teresa Finlay, Tjerk Jan Schuitmaker‐Warnaar, Nick Fahy, Paul Robinson, Mathieu Boudes, Ana Diaz, Elisa Ferrer, Virginie Hivert, Gabor Purman, Marie‐Laure Kürzinger, Robert A. Kroes, Claudia Hey, Jacqueline E.W. Broerse
Published 2020-02-01

A systematic literature review of evidence-based clinical practice for rare diseases: what are the perceived and real barriers for improving the evidence and how can they be overco...

by Ana Rath, Valérie Salamon, Sandra Peixoto, Virginie Hivert, Martine Laville, Berenice Segrestin, Edmund A. M. Neugebauer, Michaela Eikermann, Vittorio Bertele, Silvio Garattini, Jørn Wetterslev, Rita Banzi, Janus C. Jakobsen, Snezana Djurisic, Christine Kubiak, Jacques Demotes-Mainard, Christian Gluud
Published 2017-11-01