Adeno-Associated Viral Vectors as a Tool for Large Gene Delivery to the Retina

Gene therapy using adeno-associated viral (AAV) vectors currently represents the most promising approach for the treatment of many inherited retinal diseases (IRDs), given AAV’s ability to efficiently deliver therapeutic genes to both photoreceptors and retinal pigment epithelium, and thei...

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Bibliographic Details
Main Author: Ivana Trapani
Format: Article
Language:English
Published: MDPI AG 2019-04-01
Series:Genes
Subjects:
AAV
Online Access:https://www.mdpi.com/2073-4425/10/4/287