Taliglucerase alfa: safety and efficacy across 6 clinical studies in adults and children with Gaucher disease

Taliglucerase alfa: safety and efficacy across 6 clinical studies in adults and children with Gaucher disease

Abstract Taliglucerase alfa is an enzyme replacement therapy (ERT) approved for treatment of adult and paediatric patients with Type 1 Gaucher disease (GD) in several countries and the first plant cell–expressed recombinant therapeutic protein approved by the US Food and Drug Administration for huma...

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Bibliographic Details
Main Authors: Ari Zimran, Michael Wajnrajch, Betina Hernandez, Gregory M. Pastores
Format: Article
Language:English
Published: BMC 2018-02-01
Series:Orphanet Journal of Rare Diseases
Subjects:
Anaemia
Enzyme replacement therapy
Gaucher disease
Imiglucerase
Hepatomegaly
Paediatrics
Online Access:http://link.springer.com/article/10.1186/s13023-018-0776-8

Internet

http://link.springer.com/article/10.1186/s13023-018-0776-8

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