Relationship Between Patient-Reported Outcomes and Clinical Outcomes in Patients With Morquio A Syndrome

This cross-sectional analysis assessed the correlation between patient-reported outcomes (PROs) and clinical outcomes in 24 German patients with Morquio A. Clinical outcomes included 6-minute walk test (6MWT), 3-minute stair climb (3MSC) test, and joint range of motion as measures for endurance/mobi...

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Bibliographic Details
Main Authors: Christina Lampe MD, Mohit Jain PhD, Andrew Olaye PhD, Bianca Meesen MSc, Celeste Decker MD, Eugen Mengel MD
Format: Article
Language:English
Published: SciELO 2015-04-01
Series:Journal of Inborn Errors of Metabolism and Screening
Online Access:https://doi.org/10.1177/2326409815576188