Moving neuromuscular disorders research forward: from novel models to clinical studies

Neuromuscular disorders (NMDs) encompass a diverse group of genetic diseases characterized by loss of muscle functionality. Despite extensive efforts to develop therapies, no curative treatment exists for any of the NMDs. For multiple disorders, however, therapeutic strategies are currently being te...

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Bibliographic Details
Main Authors: Maaike van Putten, Julija Hmeljak, Annemieke Aartsma-Rus, James J. Dowling
Format: Article
Language:English
Published: The Company of Biologists 2020-02-01
Series:Disease Models & Mechanisms
Subjects:
Online Access:http://dmm.biologists.org/content/13/2/dmm044370