A Prospective Treatment Option for Lysosomal Storage Diseases: CRISPR/Cas9 Gene Editing Technology for Mutation Correction in Induced Pluripotent Stem Cells
Ease of design, relatively low cost and a multitude of gene-altering capabilities have all led to the adoption of the sophisticated and yet simple gene editing system: clustered regularly interspaced short palindromic repeats/CRISPR-associated protein 9 (CRISPR/Cas9). The CRISPR/Cas9 system holds pr...
Main Authors: | , |
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Format: | Article |
Language: | English |
Published: |
MDPI AG
2017-02-01
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Series: | Diseases |
Subjects: | |
Online Access: | http://www.mdpi.com/2079-9721/5/1/6 |