Cognitive Outcome of Infants with Pompe Disease Receiving Enzyme-Replacement Therapy

Researchers at University Medical Center, Rotterdam, the Netherlands, and University of Leuven, Belgium prospectively assessed cognitive function in 10 children with classic infantile Pompe disease who had been treated with enzyme-replacement therapy (ERT) since 1999.

Bibliographic Details
Main Author: J Gordon Millichap
Format: Article
Published: Pediatric Neurology Briefs Publishers 2012-06-01
Series:Pediatric Neurology Briefs
Online Access: