Current understanding and treatment of cardiac and skeletal muscle pathology in laminin-α2 chain-deficient congenital muscular dystrophy

Current understanding and treatment of cardiac and skeletal muscle pathology in laminin-α2 chain-deficient congenital muscular dystrophy

Quynh Nguyen,*,1 Kenji Rowel Q Lim,*,1 Toshifumi Yokota,1,21Department of Medical Genetics, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, AB, Canada; 2The Friends of Garrett Cumming Research & Muscular Dystrophy Canada, HM Toupin Neurological Science R...

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Bibliographic Details
Main Authors: Nguyen Q, Lim KRQ, Yokota T
Format: Article
Language:English
Published: Dove Medical Press 2019-07-01
Series:The Application of Clinical Genetics
Subjects:
LAMA2
exon skipping
genome editing
non-homologous end joining (NHEJ)
phosphorodiamidate morpholino oligomer (PMO)
CRISPR/Cas9
Online Access:https://www.dovepress.com/current-understanding-and-treatment-of-cardiac-and-skeletal-muscle-pat-peer-reviewed-article-TACG

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https://www.dovepress.com/current-understanding-and-treatment-of-cardiac-and-skeletal-muscle-pat-peer-reviewed-article-TACG

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