A Novel Retinal Gene Therapy Strategy for Batten Disease and Beyond

A Novel Retinal Gene Therapy Strategy for Batten Disease and Beyond

Batten Disease is a fatal lysosomal storage disorder characterized by cognitive and [...]

Bibliographic Details
Main Authors: Maura Schwartz, Alex Campbell, Joseph Caporale, Megan Baird, Isabella Palazzo, Shibi Likhite, Andrew Fischer, Kathrin Meyer
Format: Article
Language:English
Published: MDPI AG 2021-03-01
Series:Proceedings
Subjects:
ret and a
neuraminidase
AAV9
gene therapy
Batten Disease
Online Access:https://www.mdpi.com/2504-3900/71/1/5

Internet

https://www.mdpi.com/2504-3900/71/1/5

Similar Items