CRISPR-Cas9 for in vivo Gene Therapy: Promise and Hurdles

Owing to its easy-to-use and multiplexing nature, the genome editing tool CRISPR-Cas9 (clustered regularly interspaced short palindromic repeats (CRISPR) associated nuclease 9) is revolutionizing many areas of medical research and one of the most amazing areas is its gene therapy potentials. Previou...

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Bibliographic Details
Main Authors: Wei-Jing Dai, Li-Yao Zhu, Zhong-Yi Yan, Yong Xu, Qi-Long Wang, Xiao-Jie Lu
Format: Article
Language:English
Published: Elsevier 2016-01-01
Series:Molecular Therapy: Nucleic Acids
Online Access:http://www.sciencedirect.com/science/article/pii/S2162253117300586