Validation of Motor Outcome Measures in Myotonic Dystrophy Type 2

Introduction: Myotonic dystrophy type 2 (DM2) lacks disease-specific, validated, motor outcome measures (OMs), and patients' reported outcomes (PROs). This represents a limit for the monitoring of disease progression and treatment response. Our aim was to identify the most appropriate OMs to be...

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Bibliographic Details
Main Authors: Federica Montagnese, Emanuele Rastelli, Nina Khizanishvili, Roberto Massa, Kristina Stahl, Benedikt Schoser
Format: Article
Language:English
Published: Frontiers Media S.A. 2020-04-01
Series:Frontiers in Neurology
Subjects:
DM2
Online Access:https://www.frontiersin.org/article/10.3389/fneur.2020.00306/full