Viral Vector-Mediated Antisense Therapy for Genetic Diseases

RNA plays complex roles in normal health and disease and is becoming an important target for therapeutic intervention; accordingly, therapeutic strategies that modulate RNA function have gained great interest over the past decade. Antisense oligonucleotides (AOs) are perhaps the most promising strat...

Full description

Bibliographic Details
Main Authors: Marine Imbert, Gabriella Dias-Florencio, Aurélie Goyenvalle
Format: Article
Language:English
Published: MDPI AG 2017-01-01
Series:Genes
Subjects:
Online Access:http://www.mdpi.com/2073-4425/8/2/51