Role of elosulfase alfa in mucopolysaccharidosis IVA
Debra S Regier, Pranoot Tanpaiboon Division of Genetics and Metabolism, Children’s National Medical Center, Washington, DC, USA Abstract: Mucopolysaccharidosis type IVA (MPS IVA or Morquio A) is an autosomal recessive lysosomal storage disease which results in a striking skeletal...
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| Format: | Article |
| Language: | English |
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Dove Medical Press
2016-06-01
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| Series: | The Application of Clinical Genetics |
| Subjects: | |
| Online Access: | https://www.dovepress.com/role-of-elosulfase-alfa-in-mucopolysaccharidosis-iva-peer-reviewed-article-TACG |