Current and future alternative therapies for beta-thalassemia major

Beta-thalassemia is a group of frequent genetic disorders resulting in the synthesis of little or no β-globin chains. Novel approaches are being developed to correct the resulting α/β-globin chain imbalance, in an effort to move beyond the palliative management of this disease and the complications...

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Bibliographic Details
Main Authors: Edouard de Dreuzy, Kanit Bhukhai, Philippe Leboulch, Emmanuel Payen
Format: Article
Language:English
Published: Elsevier 2016-02-01
Series:Biomedical Journal
Subjects:
Online Access:http://www.sciencedirect.com/science/article/pii/S2319417016000172