Molecular Strategies for RPGR Gene Therapy
Mutations affecting the <i>Retinitis Pigmentosa GTPase Regulator </i>(<i>RPGR</i>)<i> </i>gene are the commonest cause of X-linked and recessive retinitis pigmentosa (RP), accounting for 10%−20% of all cases of RP. The phenotype is one of the most severe...
| Main Authors: | , , , |
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| Format: | Article |
| Language: | English |
| Published: |
MDPI AG
2019-09-01
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| Series: | Genes |
| Subjects: | |
| Online Access: | https://www.mdpi.com/2073-4425/10/9/674 |