Overview of Approaches to Mitochondrial Disease Therapy
Mitochondrial respiratory chain diseases are the most prevalent group of inherited neurometabolic disorders and are clinically, biochemically, and genetically heterogeneous. They may present at any stage of life and often manifest with severe multisystem disease, although single organ involvement is...
| Main Authors: | , |
|---|---|
| Format: | Article |
| Language: | English |
| Published: |
SciELO
2018-01-01
|
| Series: | Journal of Inborn Errors of Metabolism and Screening |
| Online Access: | https://doi.org/10.1177/2326409817752960 |