Do we always need to treat patients with spinal muscular atrophy? A personal view and experience

Do we always need to treat patients with spinal muscular atrophy? A personal view and experience

Abstract Background We report the clinical outcomes observed in our patients with SMA type 1 or 2 receiving nusinersen, and we comment on the ethical implications of this treatment, in line with our results and those reported by Audic et al. in their analysis published in the Orphanet Journal of Rar...

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Bibliographic Details
Main Authors: Caterina Agosto, Eleonora Salamon, Antuan Divisic, Francesca Benedetti, Luca Giacomelli, Aashni Shah, Giorgio Perilongo, Franca Benini
Format: Article
Language:English
Published: BMC 2021-02-01
Series:Orphanet Journal of Rare Diseases
Subjects:
Spinal muscular atrophy
Ethics
Palliative care
Treatment
Nusinersen
Online Access:https://doi.org/10.1186/s13023-020-01593-4

Internet

https://doi.org/10.1186/s13023-020-01593-4

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