Treosulfan-based conditioning for inborn errors of immunity

Inborn errors of immunity (IEI) are inherited disorders that lead to defects in the development and/or function of the immune system. The number of disorders that can be treated by haematopoietic stem-cell transplantation (HSCT) has increased rapidly with the advent of next-generation sequencing. Th...

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Bibliographic Details
Main Authors: Mary A. Slatter, Andrew R. Gennery
Format: Article
Language:English
Published: SAGE Publishing 2021-05-01
Series:Therapeutic Advances in Hematology
Online Access:https://doi.org/10.1177/20406207211013985