An open-label clinical trial of agalsidase alfa enzyme replacement therapy in children with Fabry disease who are naïve to enzyme replacement therapy
Ozlem Goker-Alpan,1 Nicola Longo,2 Marie McDonald,3 Suma P Shankar,4,5 Raphael Schiffmann,6 Peter Chang,7 Yinghua Shen,7 Arian Pano7 1Lysosomal Disorders Unit, Fairfax, VA, 2University of Utah, Salt Lake City, UT, 3Department of Pediatrics, Duke University, Durham, NC, 4Department of Ophthalmology,...
Main Authors: | , , , , , , , |
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Format: | Article |
Language: | English |
Published: |
Dove Medical Press
2016-05-01
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Series: | Drug Design, Development and Therapy |
Subjects: | |
Online Access: | https://www.dovepress.com/an-open-label-clinical-trial-of-agalsidase-alfa-enzyme-replacement-the-peer-reviewed-article-DDDT |