Data from subjects receiving intrathecal laronidase for cervical spinal stenosis due to mucopolysaccharidosis type I

Five subjects with mucopolysaccharidosis type I and symptomatic cervical spinal stenosis received intrathecal laronidase in a 4-month pilot study and/or a 12-month extension study [1]. Clinical descriptions of study subjects, nonserious adverse events, individual data tables, and scoring system meth...

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Bibliographic Details
Main Authors: P.I. Dickson, I. Kaitila, P. Harmatz, A. Mlikotic, A.H. Chen, A. Victoroff, M.B. Passage, J. Madden, S.Q. Le, D.E. Naylor
Format: Article
Language:English
Published: Elsevier 2015-12-01
Series:Data in Brief
Online Access:http://www.sciencedirect.com/science/article/pii/S2352340915001602