The efficacy and safety of nusinersen within the expanded access program in Russia
Introduction. Spinal muscular atrophy is a severe neuromuscular disease characterized by rapid progression of muscle weakness and early death. Pathogenetic therapy with nusinersen can significantly change the course of the disease and enable the patient to acquire new skills. The study of the effica...
Main Authors: | , , , , , , , , , , , , |
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Format: | Article |
Language: | Russian |
Published: |
ABV-press
2020-12-01
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Series: | Nervno-Myšečnye Bolezni |
Subjects: | |
Online Access: | https://nmb.abvpress.ru/jour/article/view/396 |