CNS-targeted Gene Therapy in Globoid Cell Leukodystrophy
博士 === 國立臺北科技大學 === 工程科技研究所 === 101 === Globoid cell leukodystrophy (GLD) is a devastating lysosomal storage disease caused by deficiency of the enzyme galactocerebrosidase (GALC). Currently, there is no definite cure for the GLD. Several attempts with CNS-directed gene therapy in twitcher mice (a m...
| Main Authors: | , |
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| Other Authors: | |
| Format: | Others |
| Language: | en_US |
| Published: |
2013
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| Online Access: | http://ndltd.ncl.edu.tw/handle/k5zrm2 |