Two-way Approach to Spinal Muscular Atrophy Therapy Development
Spinal muscular atrophy (SMA) is the most commonly inherited neurodegenerative disease that leads to infant mortality worldwide. There are no known cures for SMA, but small increase in protein levels of SMN can be beneficial. We have developed adenoviral (Ad) vectors that express a human transgene o...
| Main Author: | |
|---|---|
| Other Authors: | |
| Language: | en |
| Published: |
Université d'Ottawa / University of Ottawa
2013
|
| Subjects: | |
| Online Access: | http://hdl.handle.net/10393/26168 http://dx.doi.org/10.20381/ruor-3249 |