Who should be eligible for gene therapy clinical trials in red blood cell pyruvate kinase deficiency (PKD)?: Toward an expanded definition of severe PKD

Bibliographic Details
Main Authors: Barcellini, W. (Author), Bianchi, P. (Author), Glader, B. (Author), Grace, R.F (Author), López Lorenzo, J.L (Author), Navarro Ordoñez, S. (Author), Nicoletti, E. (Author), Schwartz, J.D (Author), Segovia, J.C (Author), Sevilla, J. (Author), Shah, A.J (Author), Zanella, A. (Author)
Format: Article
Language:English
Published: John Wiley and Sons Inc 2022
Subjects:
Online Access:View Fulltext in Publisher