Predictors of growth patterns in children with mucopolysaccharidosis I after haematopoietic stem cell transplantation

Predictors of growth patterns in children with mucopolysaccharidosis I after haematopoietic stem cell transplantation

Mucopolysaccharidosis type I (MPS I) is an autosomal-recessive metabolic disorder caused by an enzyme deficiency of lysosomal alpha-l-iduronidase (IDUA). Haematopoietic stem cell transplantation (HSCT) is the therapeutic option of choice in MPS I patients younger than 2.5 years, which has a positive...

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Bibliographic Details
Main Authors: Aries, C. (Author), Beier, R. (Author), Das, A.M (Author), Grigull, L. (Author), Hennermann, J.B (Author), Maecker-Kolhoff, B. (Author), Maier, S. (Author), Sauer, M. (Author), Zivicnjak, M. (Author)
Format: Article
Language:English
Published: John Wiley and Sons Inc 2022
Subjects:
anthropometry
children
growth pattern
haematopoietic stem cell transplantation
mucopolysaccharidosis I
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