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1by Stefan Radtke, Dnyanada Pande, Margaret Cui, Anai M. Perez, Yan-Yi Chan, Mark Enstrom, Stefanie Schmuck, Andrew Berger, Tom Eunson, Jennifer E. Adair, Hans-Peter Kiem“...Molecular Therapy: Methods & Clinical Development...”
Published 2020-09-01
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2by Yan Yang, Saiaditya Badeti, Hsiang-chi Tseng, Minh Tuyet Ma, Ting Liu, Jie-Gen Jiang, Chen Liu, Dongfang Liu“...Molecular Therapy: Methods & Clinical Development...”
Published 2020-09-01
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3by Huiying Gu, Wei Jiang, Nan You, Xiaobing Huang, Yuming Li, Xuehui Peng, Rui Dong, Zheng Wang, Yinan Zhu, Ke Wu, Jing Li, Lu Zheng“...Molecular Therapy: Methods & Clinical Development...”
Published 2020-09-01
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4by Sylvia Fong, Britta Handyside, Choong-Ryoul Sihn, Su Liu, Lening Zhang, Lin Xie, Ryan Murphy, Nicole Galicia, Bridget Yates, Wesley C. Minto, Catherine Vitelli, Danielle Harmon, Yuanbin Ru, Guoying Karen Yu, Claudia Escher, Jakob Vowinckel, Jill Woloszynek, Hassib Akeefe, Rajeev Mahimkar, Sherry Bullens, Stuart Bunting“...Molecular Therapy: Methods & Clinical Development...”
Published 2020-09-01
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5by Selami Demirci, Bjorg Gudmundsdottir, Quan Li, Juan J. Haro-Mora, Tina Nassehi, Claire Drysdale, Morgan Yapundich, Jackson Gamer, Fayaz Seifuddin, John F. Tisdale, Naoya Uchida“...Molecular Therapy: Methods & Clinical Development...”
Published 2020-06-01
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6by Dominik Wrona, Oleksandr Pastukhov, Robert S. Pritchard, Federica Raimondi, Joëlle Tchinda, Martin Jinek, Ulrich Siler, Janine Reichenbach“...Molecular Therapy: Methods & Clinical Development...”
Published 2020-06-01
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8by Muhammad Elnaggar, Anjud Al-Mohannadi, Dhanya Kizhakayil, Christophe Michel Raynaud, Sharefa Al-Mannai, Giusy Gentilcore, Igor Pavlovski, Abbirami Sathappan, Nicholas Van Panhuys, Chiara Borsotti, Antonia Follenzi, Jean-Charles Grivel, Sara Deola“...Molecular Therapy: Methods & Clinical Development...”
Published 2020-06-01
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9by Christian Hinderer, Nathan Katz, Cecilia Dyer, Tamara Goode, Julia Johansson, Peter Bell, Laura Richman, Elizabeth Buza, James M. Wilson“...Molecular Therapy: Methods & Clinical Development...”
Published 2020-06-01
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10by Giuseppa Piras, Claudia Montiel-Equihua, Yee-Ka Agnes Chan, Slawomir Wantuch, Daniel Stuckey, Derek Burke, Helen Prunty, Rahul Phadke, Darren Chambers, Armando Partida-Gaytan, Diego Leon-Rico, Neelam Panchal, Kathryn Whitmore, Miguel Calero, Sara Benedetti, Giorgia Santilli, Adrian J. Thrasher, H. Bobby Gaspar“...Molecular Therapy: Methods & Clinical Development...”
Published 2020-09-01
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11by Victoria Gálvez, Esteban Chacón-Solano, Jose Bonafont, Ángeles Mencía, Wei-Li Di, Rodolfo Murillas, Sara Llames, Asunción Vicente, Marcela Del Rio, Marta Carretero, Fernando Larcher“...Molecular Therapy: Methods & Clinical Development...”
Published 2020-09-01
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12by Josse A. Depla, Marina Sogorb-Gonzalez, Lance A. Mulder, Vivi M. Heine, Pavlina Konstantinova, Sander J. van Deventer, Katja C. Wolthers, Dasja Pajkrt, Adithya Sridhar, Melvin M. Evers“...Molecular Therapy: Methods & Clinical Development...”
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14by Junling Zhao, Yongping Yue, Aman Patel, Lakmini Wasala, Jacob F. Karp, Keqing Zhang, Dongsheng Duan, Yi Lai“...Molecular Therapy: Methods & Clinical Development...”
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15Generation of Nonhuman Primate Model of Cone Dysfunction through In Situ AAV-Mediated CNGB3 Ablation“...Molecular Therapy: Methods & Clinical Development...”
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16by Kazuki Sawamoto, Subha Karumuthil-Melethil, Shaukat Khan, Molly Stapleton, Joseph T. Bruder, Olivier Danos, Shunji Tomatsu“...Molecular Therapy: Methods & Clinical Development...”
Published 2020-09-01
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17by Martijn P.T. Ernst, Mike Broeders, Pablo Herrero-Hernandez, Esmee Oussoren, Ans T. van der Ploeg, W.W.M. Pim Pijnappel“...Molecular Therapy: Methods & Clinical Development...”
Published 2020-09-01
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18by Laetitia S. Gaspar, Magda M. Santana, Carina Henriques, Maria M. Pinto, Teresa M. Ribeiro-Rodrigues, Henrique Girão, Rui Jorge Nobre, Luís Pereira de Almeida“...Molecular Therapy: Methods & Clinical Development...”
Published 2020-09-01
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20by Saba Ghassemi, Francisco J. Martinez-Becerra, Alyssa M. Master, Sarah A. Richman, David Heo, John Leferovich, Yitao Tu, Juan Carlos García-Cañaveras, Asma Ayari, Yinan Lu, Ai Wang, Joshua D. Rabinowitz, Michael C. Milone, Carl H. June, Roddy S. O’Connor“...Molecular Therapy: Methods & Clinical Development...”
Published 2020-09-01
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