Regulated protein expression for in vivo gene therapy for neurological disorders: Progress, strategies, and issues

by Fredric P. Manfredsson, David C. Bloom, Ronald J. Mandel
Published 2012-11-01

Unexpected off-targeting effects of anti-huntingtin ribozymes and siRNA in vivo

by Eileen M. Denovan-Wright, Edgardo Rodriguez-Lebron, Alfred S. Lewin, Ronald J. Mandel
Published 2008-03-01

Neuropathological and Behavioral Consequences of Adeno-Associated Viral Vector-Mediated Continuous Intrastriatal Neurotrophin Delivery in a Focal Ischemia Model in Rats

by Gunnar Andsberg, Zaal Kokaia, Ronald L. Klein, Nicholas Muzyczka, Olle Lindvall, Ronald J. Mandel
Published 2002-03-01

Elevated GDNF levels following viral vector-mediated gene transfer can increase neuronal death after stroke in rats

by Andreas Arvidsson, Deniz Kirik, Cecilia Lundberg, Ronald J Mandel, Gunnar Andsberg, Zaal Kokaia, Olle Lindvall
Published 2003-12-01

The Future of GDNF in Parkinson's Disease

by Fredric P. Manfredsson, Nicole K. Polinski, Thyagarajan Subramanian, Nicholas Boulis, Dustin R. Wakeman, Dustin R. Wakeman, Ronald J. Mandel
Published 2020-12-01

Novel oligodendroglial alpha synuclein viral vector models of multiple system atrophy: studies in rodents and nonhuman primates

by Ronald J. Mandel, David J. Marmion, Deniz Kirik, Yaping Chu, Clifford Heindel, Thomas McCown, Steven J. Gray, Jeffrey H. Kordower
Published 2017-06-01