Exploitation of circulating CD34+ cells and non-genotoxic conditioning to overcome major limitations to treatment for autosomal recessive osteopetrosis

Bibliographic Details
Main Authors: Valentina Capo, Sara Penna, Ivan Merelli, Matteo Barcella, Serena Scala, Luca Basso-Ricci, Elena Draghici, Eleonora Palagano, Erika Zonari, Paolo Uva, Roberto Cusano, Alessandro Aiuti, Francesca Ficara, Cristina Sobacchi, Bernhard Gentner, Anna Villa
Format: Article
Language:English
Published: Elsevier 2020-10-01
Series:Bone Reports
Online Access:http://www.sciencedirect.com/science/article/pii/S2352187220303569
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spelling doaj-3d30850830924d91b2e053ab31b942472020-11-25T03:37:46ZengElsevierBone Reports2352-18722020-10-0113100596Exploitation of circulating CD34+ cells and non-genotoxic conditioning to overcome major limitations to treatment for autosomal recessive osteopetrosisValentina Capo0Sara Penna1Ivan Merelli2Matteo Barcella3Serena Scala4Luca Basso-Ricci5Elena Draghici6Eleonora Palagano7Erika Zonari8Paolo Uva9Roberto Cusano10Alessandro Aiuti11Francesca Ficara12Cristina Sobacchi13Bernhard Gentner14Anna Villa15San Raffaele Telethon Institute for Gene Therapy, IRCSS San Raffaele Scientific Institute, Milan, Italy; Corresponding author.San Raffaele Telethon Institute for Gene Therapy, IRCSS San Raffaele Scientific Institute, Milan, Italy; DIMET, University of Milano-Bicocca, Monza, ItalyInstitute for Biomedical Technologies, National Research Council, Segrate, ItalySan Raffaele Telethon Institute for Gene Therapy, IRCSS San Raffaele Scientific Institute, Milan, ItalySan Raffaele Telethon Institute for Gene Therapy, IRCSS San Raffaele Scientific Institute, Milan, ItalySan Raffaele Telethon Institute for Gene Therapy, IRCSS San Raffaele Scientific Institute, Milan, ItalySan Raffaele Telethon Institute for Gene Therapy, IRCSS San Raffaele Scientific Institute, Milan, ItalyCNR-IRGB, Milan Unit, Milan, Italy; Humanitas Clinical and Research Center - IRCCS, Rozzano, ItalySan Raffaele Telethon Institute for Gene Therapy, IRCSS San Raffaele Scientific Institute, Milan, ItalyCRS4, Science and Technology Park Polaris, Pula, ItalyCRS4, Science and Technology Park Polaris, Pula, ItalySan Raffaele Telethon Institute for Gene Therapy, IRCSS San Raffaele Scientific Institute, Milan, ItalyCNR-IRGB, Milan Unit, Milan, Italy; Humanitas Clinical and Research Center - IRCCS, Rozzano, ItalyCNR-IRGB, Milan Unit, Milan, Italy; Humanitas Clinical and Research Center - IRCCS, Rozzano, ItalySan Raffaele Telethon Institute for Gene Therapy, IRCSS San Raffaele Scientific Institute, Milan, ItalySan Raffaele Telethon Institute for Gene Therapy, IRCSS San Raffaele Scientific Institute, Milan, Italy; CNR-IRGB, Milan Unit, Milan, Italyhttp://www.sciencedirect.com/science/article/pii/S2352187220303569
collection DOAJ
language English
format Article
sources DOAJ
author Valentina Capo
Sara Penna
Ivan Merelli
Matteo Barcella
Serena Scala
Luca Basso-Ricci
Elena Draghici
Eleonora Palagano
Erika Zonari
Paolo Uva
Roberto Cusano
Alessandro Aiuti
Francesca Ficara
Cristina Sobacchi
Bernhard Gentner
Anna Villa
spellingShingle Valentina Capo
Sara Penna
Ivan Merelli
Matteo Barcella
Serena Scala
Luca Basso-Ricci
Elena Draghici
Eleonora Palagano
Erika Zonari
Paolo Uva
Roberto Cusano
Alessandro Aiuti
Francesca Ficara
Cristina Sobacchi
Bernhard Gentner
Anna Villa
Exploitation of circulating CD34+ cells and non-genotoxic conditioning to overcome major limitations to treatment for autosomal recessive osteopetrosis
Bone Reports
author_facet Valentina Capo
Sara Penna
Ivan Merelli
Matteo Barcella
Serena Scala
Luca Basso-Ricci
Elena Draghici
Eleonora Palagano
Erika Zonari
Paolo Uva
Roberto Cusano
Alessandro Aiuti
Francesca Ficara
Cristina Sobacchi
Bernhard Gentner
Anna Villa
author_sort Valentina Capo
title Exploitation of circulating CD34+ cells and non-genotoxic conditioning to overcome major limitations to treatment for autosomal recessive osteopetrosis
title_short Exploitation of circulating CD34+ cells and non-genotoxic conditioning to overcome major limitations to treatment for autosomal recessive osteopetrosis
title_full Exploitation of circulating CD34+ cells and non-genotoxic conditioning to overcome major limitations to treatment for autosomal recessive osteopetrosis
title_fullStr Exploitation of circulating CD34+ cells and non-genotoxic conditioning to overcome major limitations to treatment for autosomal recessive osteopetrosis
title_full_unstemmed Exploitation of circulating CD34+ cells and non-genotoxic conditioning to overcome major limitations to treatment for autosomal recessive osteopetrosis
title_sort exploitation of circulating cd34+ cells and non-genotoxic conditioning to overcome major limitations to treatment for autosomal recessive osteopetrosis
publisher Elsevier
series Bone Reports
issn 2352-1872
publishDate 2020-10-01
url http://www.sciencedirect.com/science/article/pii/S2352187220303569
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