Autosomal recessive osteopetrosis: mechanisms and treatments

by Sara Penna, Anna Villa, Valentina Capo
Published 2021-05-01

One Disease, Many Genes: Implications for the Treatment of Osteopetroses

by Sara Penna, Sara Penna, Valentina Capo, Eleonora Palagano, Eleonora Palagano, Cristina Sobacchi, Cristina Sobacchi, Anna Villa, Anna Villa
Published 2019-02-01

Non-genotoxic conditioning to overcome transplant-related toxicity in oc/oc osteopetrotic mouse model

by Valentina Capo, Sara Penna, Ludovica Santi, Andrea Cappelleri, Stefano Mantero, Eugenio Scanziani, Anna Villa
Published 2021-04-01

Investigation of the bone damage in mucopolysaccharidosis type I Hurler Syndrome: Pathophysiological mechanisms and the impact of ex vivo gene therapy

by Sara Penna, Stefania Crippa, Valentina Capo, Ludovica Santi, Roberto Bosotti, Mara Riminucci, Alessandro Corsi, Marta Serafini, Bernhard Gentner, Alessandro Aiuti, Maria Ester Bernardo, Anna Villa
Published 2020-10-01

Exploitation of circulating CD34+ cells and non-genotoxic conditioning to overcome major limitations to treatment for autosomal recessive osteopetrosis

by Valentina Capo, Sara Penna, Ivan Merelli, Matteo Barcella, Serena Scala, Luca Basso-Ricci, Elena Draghici, Eleonora Palagano, Erika Zonari, Paolo Uva, Roberto Cusano, Alessandro Aiuti, Francesca Ficara, Cristina Sobacchi, Bernhard Gentner, Anna Villa
Published 2020-10-01