Investigation of the bone damage in mucopolysaccharidosis type I Hurler Syndrome: Pathophysiological mechanisms and the impact of ex vivo gene therapy

by Sara Penna, Stefania Crippa, Valentina Capo, Ludovica Santi, Roberto Bosotti, Mara Riminucci, Alessandro Corsi, Marta Serafini, Bernhard Gentner, Alessandro Aiuti, Maria Ester Bernardo, Anna Villa
Published 2020-10-01