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1by Sarah Bird, Efthymios Hadjimichael, Atul Mehta, Uma Ramaswami, Derralynn HughesGet full text
Published 2017-09-01
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3by Michael Beck, Derralynn Hughes, Christoph Kampmann, Sylvain Larroque, Atul Mehta, Guillem Pintos-Morell, Uma Ramaswami, Michael West, Anna Wijatyk, Roberto GiuglianiGet full text
Published 2015-06-01
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4by Daniel G. Bichet, Roser Torra, Eric Wallace, Derralynn Hughes, Roberto Giugliani, Nina Skuban, Eva Krusinska, Ulla Feldt-Rasmussen, Raphael Schiffmann, Kathy NichollsGet full text
Published 2021-09-01
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5by Maureen Cleary, James Davison, Rachel Gould, Tarekegn Geberhiwot, Derralynn Hughes, Jean Mercer, Alexandra Morrison, Elaine Murphy, Saikat Santra, James Jarrett, Swati Mukherjee, Karolina M. StepienGet full text
Published 2021-01-01
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6by Sanne J. van der Veen, Wytze J. Vlietstra, Laura van Dussen, André B.P. van Kuilenburg, Marcel G. W. Dijkgraaf, Malte Lenders, Eva Brand, Christoph Wanner, Derralynn Hughes, Perry M. Elliott, Carla E. M. Hollak, Mirjam LangeveldGet full text
Published 2020-08-01
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7A study on the safety and efficacy of reveglucosidase alfa in patients with late-onset Pompe diseaseby Barry J. Byrne, Tarekegn Geberhiwot, Bruce A. Barshop, Richard Barohn, Derralynn Hughes, Drago Bratkovic, Claude Desnuelle, Pascal Laforet, Eugen Mengel, Mark Roberts, Peter Haroldsen, Kristin Reilley, Kala Jayaram, Ke Yang, Liron Walsh, on behalf of the POM-001/002 InvestigatorsGet full text
Published 2017-08-01
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9by Richard D Neal, Amitava Banerjee, Deenan Pillay, Vahe Nafilyan, Clare Turnbull, Harry Hemingway, Bryan Williams, Mark Lawler, Spiros Denaxas, Kathy Pritchard-Jones, Mahdad Noursadeghi, Richard Sullivan, Graham R Foster, Ben Humberstone, Alvina G Lai, Laura Pasea, Wai Hoong Chang, Michail Katsoulis, David Linch, Derralynn Hughes, Martin D Forster, Natalie K Fitzpatrick, Kathryn Boyd, Tariq Enver, Matt Cooper, Charlie DavieGet full text
Published 2020-11-01
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