Investigation of the bone damage in mucopolysaccharidosis type I Hurler Syndrome: Pathophysiological mechanisms and the impact of ex vivo gene therapy

Bibliographic Details
Main Authors: Sara Penna, Stefania Crippa, Valentina Capo, Ludovica Santi, Roberto Bosotti, Mara Riminucci, Alessandro Corsi, Marta Serafini, Bernhard Gentner, Alessandro Aiuti, Maria Ester Bernardo, Anna Villa
Format: Article
Language:English
Published: Elsevier 2020-10-01
Series:Bone Reports
Online Access:http://www.sciencedirect.com/science/article/pii/S2352187220303570